Researchers at the University of Valencia in Spain recently identified a new way to block the genetic change that causes myotonic dystrophy Type 1. The research is summarised in an article which you can read on the Muscular Dystrophy Campaign website using this link: New lead for myotonic dystrophy treatment
The same article refers to the research being carried out in Rochester, USA, by Professor Charles Thornton, and points to some similarities between the strategy being pursued there, and the recently published trials in the UK with a small group of patients with another muscular dystrophy, Duchenne's.
Professor Darren Monckton, myotonic dystrophy researcher at the University of Glasgow, describes the Spanish data as 'certainly very encouraging and if replicated in humans would be expected to be therapeutically beneficial'.
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